A Review of CRISPR Tools for Treating Usher Syndrome: Applicability, Safety, Efficiency, and In Vivo Delivery by Lauren Major, Michelle E. McClements, Robert E. MacLaren

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CRISPR-Cas9 DNA Base-Editing and Prime-Editing by Ariel Kantor, Michelle E. McClements, Robert E. MacLaren

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New CRISPR Tools to Correct Pathogenic Mutations in Usher Syndrome by Lauren Major, Michelle E. McClements, Robert E. MacLaren

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CRISPR Manipulation of Age-Related Macular Degeneration Haplotypes in the Complement System: Potential Future Therapeutic Applications/Avenues by Ahmed Salman, Michelle E. McClements, Robert E. MacLaren

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Therapy Approaches for Stargardt Disease by Elena Piotter, Michelle E McClements, Robert E MacLaren

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Insights on the Regeneration Potential of Müller Glia in the Mammalian Retina by Ahmed Salman, Michelle E. McClements, Robert E. MacLaren

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CRISPR DNA Base Editing Strategies for Treating Retinitis Pigmentosa Caused by Mutations in <i>Rhodopsin</i> by Maria Kaukonen, Michelle E. McClements, Robert E. MacLaren

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Minicircle Delivery to the Neural Retina as a Gene Therapy Approach by Federica Staurenghi, Michelle E. McClements, Ahmed Salman, Robert E. MacLaren

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Future Perspectives of Prime Editing for the Treatment of Inherited Retinal Diseases by Silja Hansen, Michelle E. McClements, Thomas J. Corydon, Robert E. MacLaren

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The Scope of Pathogenic ABCA4 Mutations Targetable by CRISPR DNA Base Editing Systems—A Systematic Review by Elena Piotter, Michelle E. McClements, Robert E. MacLaren, Robert E. MacLaren

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Accurate Quantification of AAV Vector Genomes by Quantitative PCR by Cristina Martinez-Fernandez de la Camara, Michelle E. McClements, Robert E. MacLaren

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CRISPR Interference–Potential Application in Retinal Disease by Caroline F. Peddle, Lewis E. Fry, Michelle E. McClements, Robert E. MacLaren

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Non-Viral Delivery of CRISPR/Cas Cargo to the Retina Using Nanoparticles: Current Possibilities, Challenges, and Limitations by Ahmed Salman, Ariel Kantor, Michelle E. McClements, Gemma Marfany, Sonia Trigueros, Robert E. MacLaren

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In Silico Analysis of Pathogenic <i>CRB1</i> Single Nucleotide Variants and Their Amenability to Base Editing as a Potential Lead for Therapeutic Intervention by Julia-Sophia Bellingrath, Michelle E. McClements, Maria Kaukonen, Manuel Dominik Fischer, Robert E. MacLaren

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Inclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human Retina by Maria I. Patrício, Alun R. Barnard, Harry O. Orlans, Michelle E. McClements, Robert E. MacLaren

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Analysis of Early Cone Dysfunction in an In Vivo Model of Rod-Cone Dystrophy by Mark M. Hassall, Michelle E. McClements, Alun R. Barnard, Maria I. Patrício, Sher A. Aslam, Robert E. Maclaren

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Immunomodulatory Effects of Hydroxychloroquine and Chloroquine in Viral Infections and Their Potential Application in Retinal Gene Therapy by Laurel C. Chandler, Imran H. Yusuf, Michelle E. McClements, Alun R. Barnard, Robert E. MacLaren, Kanmin Xue

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Optogenetic Gene Therapy for the Degenerate Retina: Recent Advances by Michelle E. McClements, Federica Staurenghi, Robert E. MacLaren, Robert E. MacLaren, Jasmina Cehajic-Kapetanovic, Jasmina Cehajic-Kapetanovic

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Programmable RNA editing with endogenous ADAR enzymes – a feasible option for the treatment of inherited retinal disease? by Julia-Sophia Bellingrath, Michelle E. McClements, M. Dominik Fischer, M. Dominik Fischer, Robert E. MacLaren, Robert E. MacLaren

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Characterizing the cellular immune response to subretinal AAV gene therapy in the murine retina by Laurel C. Chandler, Michelle E. McClements, Imran H. Yusuf, Cristina Martinez-Fernandez de la Camara, Robert E. MacLaren, Kanmin Xue

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