Therapy Approaches for Stargardt Disease Autor Elena Piotter, Michelle E McClements, Robert E MacLaren

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Insights on the Regeneration Potential of Müller Glia in the Mammalian Retina Autor Ahmed Salman, Michelle E. McClements, Robert E. MacLaren

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Future Perspectives of Prime Editing for the Treatment of Inherited Retinal Diseases Autor Silja Hansen, Michelle E. McClements, Thomas J. Corydon, Robert E. MacLaren

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The Scope of Pathogenic ABCA4 Mutations Targetable by CRISPR DNA Base Editing Systems—A Systematic Review Autor Elena Piotter, Michelle E. McClements, Robert E. MacLaren, Robert E. MacLaren

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Non-Viral Delivery of CRISPR/Cas Cargo to the Retina Using Nanoparticles: Current Possibilities, Challenges, and Limitations Autor Ahmed Salman, Ariel Kantor, Michelle E. McClements, Gemma Marfany, Sonia Trigueros, Robert E. MacLaren

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Inclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human Retina Autor Maria I. Patrício, Alun R. Barnard, Harry O. Orlans, Michelle E. McClements, Robert E. MacLaren

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Optogenetic Gene Therapy for the Degenerate Retina: Recent Advances Autor Michelle E. McClements, Federica Staurenghi, Robert E. MacLaren, Robert E. MacLaren, Jasmina Cehajic-Kapetanovic, Jasmina Cehajic-Kapetanovic

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Mirtron-mediated RNA knockdown/replacement therapy for the treatment of dominant retinitis pigmentosa Autor Harry O. Orlans, Michelle E. McClements, Alun R. Barnard, Cristina Martinez-Fernandez de la Camara, Robert E. MacLaren

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Programmable RNA editing with endogenous ADAR enzymes – a feasible option for the treatment of inherited retinal disease? Autor Julia-Sophia Bellingrath, Michelle E. McClements, M. Dominik Fischer, M. Dominik Fischer, Robert E. MacLaren, Robert E. MacLaren

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Characterizing the cellular immune response to subretinal AAV gene therapy in the murine retina Autor Laurel C. Chandler, Michelle E. McClements, Imran H. Yusuf, Cristina Martinez-Fernandez de la Camara, Robert E. MacLaren, Kanmin Xue

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Comparison of CRISPR-Cas13b RNA base editing approaches for USH2A-associated inherited retinal degeneration Autor Lewis E. Fry, Lauren Major, Ahmed Salman, Lucy A. McDermott, Jun Yang, Andrew J. King, Michelle E. McClements, Robert E. MacLaren

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Enhancement of Adeno-Associated Virus-Mediated Gene Therapy Using Hydroxychloroquine in Murine and Human Tissues Autor Laurel C. Chandler, Alun R. Barnard, Sarah L. Caddy, Maria I. Patrício, Michelle E. McClements, Howell Fu, Cristina Rada, Robert E. MacLaren, Kanmin Xue

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AAV2/8 Anti-angiogenic Gene Therapy Using Single-Chain Antibodies Inhibits Murine Choroidal Neovascularization Autor Chris P. Hughes, Neil M.J. O’Flynn, Maureen Gatherer, Michelle E. McClements, Jennifer A. Scott, Robert E. MacLaren, Srinivas Goverdhan, Martin J. Glennie, Andrew J. Lotery

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Single-cell transcriptomic analysis of retinal immune regulation and blood-retinal barrier function during experimental autoimmune uveitis Autor Joel Quinn, Ahmed Salman, Christopher Paluch, Matthew Jackson-Wood, Michelle E. McClements, Jian Luo, Simon J. Davis, Richard J. Cornall, Robert E. MacLaren, Calliope A. Dendrou, Kanmin Xue

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AAV2-mediated gene therapy for Bietti crystalline dystrophy provides functional CYP4V2 in multiple relevant cell models Autor Jiang-Hui Wang, Grace E. Lidgerwood, Maciej Daniszewski, Monica L. Hu, Georgina E. Roberts, Raymond C. B. Wong, Sandy S. C. Hung, Michelle E. McClements, Alex W. Hewitt, Alice Pébay, Doron G. Hickey, Thomas L. Edwards

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