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Safety and efficacy of viltolarsen in ambulatory and nonambulatory males with Duchenne muscular dystrophy by Amy D. Harper, Haluk Topaloglu, Eugenio Mercuri, Vasiliy Suslov, Liwen Wu, Cigdem Y. Ayanoglu, Michael Tansey, Michelle L. Previtera, Robert A. Crozier, Leslie Magnus, Paula R. Clemens
Published 2024-10-01
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