Manufacturing of recombinant adeno-associated viral vectors for clinical trials by Nathalie Clément, Joshua C Grieger

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Pharmacology of Recombinant Adeno-associated Virus Production by Magalie Penaud-Budloo, Achille François, Nathalie Clément, Eduard Ayuso

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The comparability tales: A phase-appropriate roadmap for CGT drug product development by Nathalie Clément, Sadik H. Kassim, Daniel Leblanc, Katy Spink, John Tomtishen

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A scalable method for the production of high-titer and high-quality adeno-associated type 9 vectors using the HSV platform by Laura Adamson-Small, Mark Potter, Darin J Falk, Brian Cleaver, Barry J Byrne, Nathalie Clément

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Prevalence of Human Bocavirus in Human Tonsils and Adenoids by Nathalie Clément, Gino Battaglioli, Ryan L. Jensen, Bruce C. Schnepp, Philip R. Johnson, Kirsten St. George, R. Michael Linden

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Comparison of highly pure rAAV9 vector stocks produced in suspension by PEI transfection or HSV infection reveals striking quantitative and qualitative differences by Prasad D. Trivedi, Chenghui Yu, Payel Chaudhuri, Evan J. Johnson, Tina Caton, Laura Adamson, Barry J. Byrne, Nicole K. Paulk, Nathalie Clément

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A simplified purification protocol for recombinant adeno-associated virus vectors by Mark Potter, Bridget Lins, Mario Mietzsch, Regine Heilbronn, Kim Van Vliet, Paul Chipman, Mavis Agbandje-McKenna, Brian D Cleaver, Nathalie Clément, Barry J Byrne, Sergei Zolotukhin

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Micro-dystrophin AAV Vectors Made by Transient Transfection and Herpesvirus System Are Equally Potent in Treating mdx Mouse Muscle Disease by Chady H. Hakim, Nathalie Clément, Lakmini P. Wasala, Hsiao T. Yang, Yongping Yue, Keqing Zhang, Kasun Kodippili, Laura Adamson-Small, Xiufang Pan, Joel S. Schneider, N. Nora Yang, Jeffrey S. Chamberlain, Barry J. Byrne, Dongsheng Duan

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Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation by Manuela Corti, Barry J. Byrne, Dominic J. Gessler, Grace Thompson, Samantha Norman, Jenna Lammers, Kirsten E. Coleman, Cristina Liberati, Melissa E. Elder, Maria L. Escolar, Ibrahim S. Tuna, Clementina Mesaros, Gary I. Kleiner, Deborah S. Barbouth, Heather L. Gray-Edwards, Nathalie Clement, Brian D. Cleaver, Guangping Gao

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Identification of pathway-biased and deleterious melatonin receptor mutants in autism spectrum disorders and in the general population. by Pauline Chaste, Nathalie Clement, Oriane Mercati, Jean-Luc Guillaume, Richard Delorme, Hany Goubran Botros, Cécile Pagan, Samuel Périvier, Isabelle Scheid, Gudrun Nygren, Henrik Anckarsäter, Maria Rastam, Ola Ståhlberg, Carina Gillberg, Emilie Serrano, Nathalie Lemière, Jean Marie Launay, Marie Christine Mouren-Simeoni, Marion Leboyer, Christopher Gillberg, Ralf Jockers, Thomas Bourgeron

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The orphan GPR50 receptor promotes constitutive TGFβ receptor signaling and protects against cancer development by Stefanie Wojciech, Raise Ahmad, Zakia Belaid-Choucair, Anne-Sophie Journé, Sarah Gallet, Julie Dam, Avais Daulat, Delphine Ndiaye-Lobry, Olivier Lahuna, Angeliki Karamitri, Jean-Luc Guillaume, Marcio Do Cruzeiro, François Guillonneau, Anastasia Saade, Nathalie Clément, Thomas Courivaud, Nawel Kaabi, Kenjiro Tadagaki, Philippe Delagrange, Vincent Prévot, Olivier Hermine, Céline Prunier, Ralf Jockers

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