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Givinostat for Becker muscular dystrophy: A randomized, placebo-controlled, double-blind study by Giacomo P. Comi, Giacomo P. Comi, Erik H. Niks, Erik H. Niks, Krista Vandenborne, Claudia M. Cinnante, Hermien E. Kan, Hermien E. Kan, Rebecca J. Willcocks, Daniele Velardo, Francesca Magri, Michela Ripolone, Jules J. van Benthem, Nienke M. van de Velde, Nienke M. van de Velde, Simone Nava, Laura Ambrosoli, Sara Cazzaniga, Paolo U. Bettica
Published 2023-01-01
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Preserved thenar muscles in non‐ambulant Duchenne muscular dystrophy patients by Karin J. Naarding, Kevin R. Keene, Aashley S.D. Sardjoe Mishre, Thom T.J. Veeger, Nienke M. van deVelde, Arina J. Prins, Jedrzej Burakiewicz, Jan J.G.M. Verschuuren, Menno van derHolst, Erik H. Niks, Hermien E. Kan
Published 2021-06-01
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Diffusion‐tensor magnetic resonance imaging captures increased skeletal muscle fibre diameters in Becker muscular dystrophy by Donnie Cameron, Tooba Abbassi‐Daloii, Laura G.M. Heezen, Nienke M. van deVelde, Zaïda Koeks, Thom T.J. Veeger, Melissa T. Hooijmans, Salma elAbdellaoui, Sjoerd G. vanDuinen, Jan J.G.M. Verschuuren, Maaike vanPutten, Annemieke Aartsma‐Rus, Vered Raz, Pietro Spitali, Erik H. Niks, Hermien E. Kan
Published 2023-06-01
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