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Precision Editing as a Therapeutic Approach for β-Hemoglobinopathies by Kiriaki Paschoudi, Evangelia Yannaki, Nikoletta Psatha
Published 2023-05-01
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P1358: MINING THE GENOME FOR ERYTHROID SPECIFIC ENHANCERS TO OPTIMIZE GENE THERAPY VECTORS FOR BETA-HEMOGLOBINOPATHIES by Kiriaki Paschoudi, Grigorios Georgolopoulos, Pavel Sova, Ioannis Ninos Vasiloudis, Alexandra Kirtsou, Fotios Papadopoulos, Mineo Iwata, Hau Wang, Christina Beta, Thalia Papayannopoulou, John Stamatoyannopoulos, Evangelia Yannaki, Jeff Viestra, Nikoletta Psatha
Published 2023-08-01
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