Polycystic Kidney Disease Ryanodine Receptor Domain (PKDRR) Proteins in Oomycetes by Limian Zheng, Barbara Doyle Prestwich, Patrick T. Harrison, John J. Mackrill

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Cas9/gRNA targeted excision of cystic fibrosis-causing deep-intronic splicing mutations restores normal splicing of CFTR mRNA. by David J Sanz, Jennifer A Hollywood, Martina F Scallan, Patrick T Harrison

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In Vitro and In Vivo Models to Study Nephropathic Cystinosis by Pang Yuk Cheung, Patrick T. Harrison, Alan J. Davidson, Jennifer A. Hollywood

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Mutation-class dependent signatures outweigh disease-associated processes in cystic fibrosis cells by Lúcia Santos, Rui Nascimento, Aires Duarte, Violeta Railean, Margarida D. Amaral, Patrick T. Harrison, Margarida Gama-Carvalho, Carlos M. Farinha

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Therapeutic Potential of a Scorpion Venom-Derived Antimicrobial Peptide and Its Homologs Against Antibiotic-Resistant Gram-Positive Bacteria by Gaomin Liu, Fan Yang, Fangfang Li, Zhongjie Li, Yange Lang, Bingzheng Shen, Yingliang Wu, Wenxin Li, Patrick L. Harrison, Peter N. Strong, Yingqiu Xie, Keith Miller, Zhijian Cao, Zhijian Cao, Zhijian Cao

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Adenine base editing with engineered virus-like particles rescues the CFTR mutation G542X in patient-derived intestinal organoids by Lucia Nicosia, Iwona Pranke, Roberta V. Latorre, Joss B. Murray, Lisa Lonetti, Kader Cavusoglu-Doran, Elise Dreano, James P. Costello, Michael Carroll, Paola Melotti, Claudio Sorio, Isabelle Sermet-Gaudelus, Martina F. Scallan, Patrick T. Harrison

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