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Azacytidine Treatment for VEXAS Syndrome by Marc H. G. P. Raaijmakers, Maud Hermans, Anna Aalbers, Melissa Rijken, Virgil A. S. H. Dalm, Paul van Daele, Peter J. M. Valk
Published 2021-12-01
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Curation and expansion of the Human Phenotype Ontology for systemic autoinflammatory diseases improves phenotype-driven disease-matching by Willem Maassen, Geertje Legger, Ovgu Kul Cinar, Paul van Daele, Paul van Daele, Marco Gattorno, Brigitte Bader-Meunier, Brigitte Bader-Meunier, Carine Wouters, Tracy Briggs, Tracy Briggs, Lennart Johansson, Joeri van der Velde, Morris Swertz, Ebun Omoyinmi, Esther Hoppenreijs, Alexandre Belot, Alexandre Belot, Despina Eleftheriou, Roberta Caorsi, Florence Aeschlimann, Florence Aeschlimann, Guilaine Boursier, Paul Brogan, Matthias Haimel, Marielle van Gijn
Published 2023-09-01
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P1017: REDUCTIONS IN INDOLENT SYSTEMIC MASTOCYTOSIS BIOMARKER BURDEN WITH AVAPRITINIB IN THE REGISTRATIONAL, DOUBLE-BLIND PLACEBO-CONTROLLED PIONEER TRIAL by Jason Gotlib, Mariana Castells, Hanneke Oude Elberink, Frank Siebenhaar, Karin Hartmann, Sigurd Broesby-Olsen, Tracy I. George, Jens Panse, Ivan Alvarez-Twose, Deepti Radia, Tsewang Tashi, Cristina Bulai Livideanu, Vito Sabato, Paul Van Daele, Sonia Cerquozzi, Ingunn Dybedal, Andreas Reiter, Celalettin Ustun, Philippe Schafhausen, Prithviraj Bose, Daniel J. Deangelo, Lindsay Rein, Pankit Vachhani, Massimo Triggiani, Mark Rafferty, Nauman Butt, Stephen Oh, Friederike Wortmann, Johanna Ungerstedt, Minakshi Taparia, Andrew T. Kuykendall, Cecilia Arana Yi, Mattias Mattsson, William Shomali, Matthew Giannetti, Ilda Bidollari, Hui-Min Lin, Robyn Scherber, Maria Roche, Cem Akin, Marcus Maurer
Published 2023-08-01
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