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Novel hybrid silicon-lipid nanoparticles deliver a siRNA to cure autosomal dominant osteopetrosis in mice. Implications for gene therapy in humans by Antonio Maurizi, Piergiorgio Patrizii, Anna Teti, Flavia Maria Sutera, Paulina Baran-Rachwalska, Chris Burns, Uttom Nandi, Michael Welsh, Nissim Torabi-Pour, Ashkan Dehsorkhi, Suzanne Saffie-Siebert
Published 2023-09-01
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