Showing 1 - 6 results of 6 for search 'Perry B Shieh', query time: 0.03s Refine Results
  1. 1
    Healthcare Utilization, Costs of Care, and Mortality Among Patients With Spinal Muscular Atrophy

    Healthcare Utilization, Costs of Care, and Mortality Among Patients With Spinal Muscular Atrophy by Hiangkiat Tan, Tao Gu, Er Chen, Rajeshwari Punekar, Perry B. Shieh

    Published 2019-12-01
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    Article
  2. 2
    The Last Mile: DSCSA Solution Through Blockchain Technology: Drug Tracking, Tracing, and Verification at the Last Mile of the Pharmaceutical Supply Chain with BRUINchain

    The Last Mile: DSCSA Solution Through Blockchain Technology: Drug Tracking, Tracing, and Verification at the Last Mile of the Pharmaceutical Supply Chain with BRUINchain by William Chien, Josenor de Jesus, Ben Taylor, Victor Dods, Leo Alekseyev, Diane Shoda, Perry B. Shieh

    Published 2020-03-01
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  3. 3
    Disease progression rates in ambulatory Duchenne muscular dystrophy by steroid type, patient age and functional status

    Disease progression rates in ambulatory Duchenne muscular dystrophy by steroid type, patient age and functional status by Craig M McDonald, Jessica R Marden, Perry B Shieh, Brenda L Wong, Henry Lane, Adina Zhang, Ha Nguyen, Molly Frean, Panayiota Trifillis, Karyn Koladicz, James Signorovitch

    Published 2023-02-01
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  4. 4
    O19: Integrated analyses of data from clinical trials of delandistrogene moxeparvovec gene therapy in DMD*

    O19: Integrated analyses of data from clinical trials of delandistrogene moxeparvovec gene therapy in DMD* by Erin O’Rourke, Crystal Proud, Craig Zaidman, Perry B. Shieh, Craig McDonald, John W. Day, Stefanie Mason, Maitea Guridi, Lixin Han, Lixi Yu, Carol Reid, Eddie Darton, Christoph Wandel, James Richardson, Jyoti Malhotra, Teji Singh, Louise Rodino-Klapac, Jerry Mendell

    Published 2023-01-01
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  5. 5
    Current insights in ultra-rare adenylosuccinate synthetase 1 myopathy – meeting report on the First Clinical and Scientific Conference. 3 June 2024, National Centre for Advancing Translational Science, Rockville, Maryland, the United States of America

    Current insights in ultra-rare adenylosuccinate synthetase 1 myopathy – meeting report on the First Clinical and Scientific Conference. 3 June 2024, National Centre for Advancing T... by Emma Rybalka, Hyung Jun Park, Atchayaram Nalini, Dipti Baskar, Kiran Polavarapu, Hacer Durmus, Yang Xia, Linlin Wan, Perry B. Shieh, Behzad Moghadaszadeh, Alan H. Beggs, David L. Mack, Alec S. T. Smith, Wendy Hanna-Rose, Hyder A. Jinnah, Cara A. Timpani, Min Shen, Jaymin Upadhyay, Jeffrey J. Brault, Matthew D. Hall, Naveen Baweja, Priyanka Kakkar

    Published 2024-11-01
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  6. 6
    Expression of SRP-9001 dystrophin and stabilization of motor function up to 2 years post-treatment with delandistrogene moxeparvovec gene therapy in individuals with Duchenne muscular dystrophy

    Expression of SRP-9001 dystrophin and stabilization of motor function up to 2 years post-treatment with delandistrogene moxeparvovec gene therapy in individuals with Duchenne muscu... by Jerry R. Mendell, Jerry R. Mendell, Jerry R. Mendell, Perry B. Shieh, Craig M. McDonald, Zarife Sahenk, Zarife Sahenk, Zarife Sahenk, Kelly J. Lehman, Linda P. Lowes, Linda P. Lowes, Natalie F. Reash, Megan A. Iammarino, Lindsay N. Alfano, Brenna Sabo, Jeremy D. Woods, Christy L. Skura, Howard C. Mao, Loretta A. Staudt, Danielle A. Griffin, Sarah Lewis, Shufang Wang, Rachael A. Potter, Teji Singh, Louise R. Rodino-Klapac

    Published 2023-07-01
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