Management goals of type 1 Gaucher disease in South Africa: An expert Delphi consensus document on good clinical practice. by Vernon Johan Louw, Ilanca Fraser, Pilar Giraldo

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POEMS syndrome with severe neurological damage clinically recovered with lenalidomide by José F. Tomás, Pilar Giraldo, Ramón Lecumberri, Sara Nistal

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Neutrophil extracellular traps and macrophage activation contibute to thrombosis and post-covid syndrome in SARS-CoV-2 infection by Irene Serrano-Gonzalo, Irene Serrano-Gonzalo, Irene Serrano-Gonzalo, Irene Serrano-Gonzalo, Bárbara Menéndez-Jandula, Esther Franco-García, Esther Franco-García, Esther Franco-García, Isidro Arévalo-Vargas, Isidro Arévalo-Vargas, Isidro Arévalo-Vargas, Calos Lahoz-Gil, Paz Latre, Paz Latre, Sonia Roca-Esteve, Ralf Köhler, Ralf Köhler, Ralf Köhler, Laura López de Frutos, Laura López de Frutos, Pilar Giraldo, Pilar Giraldo, Pilar Giraldo, Pilar Giraldo, Pilar Giraldo

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Advantages of digital technology in the assessment of bone marrow involvement in Gaucher's disease by Esther Valero-Tena, Esther Valero-Tena, Mercedes Roca-Espiau, Jose Verdú-Díaz, Jordi Diaz-Manera, Marcio Andrade-Campos, Marcio Andrade-Campos, Marcio Andrade-Campos, Pilar Giraldo, Pilar Giraldo

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P1662: STUDY OF THE DEVELOPMENT AND INVOLVEMENT OF NEUTROPHIL EXTRACELLULAR TRAPS (NETS) IN VASCULAR COMPLICATIONS IN LYSOSOMAL DISORDERS by Irene Serrano-Gonzalo, Sonia Roca Esteve, Carlos Lahoz, Isidro Arévalo-Vargas, Pilar Giraldo

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A novel mutation in two Spanish children with Niemann Pick disease: description of genotype, sphingomyelinase activity, phenotype and review by Pablo del Villar-Guerra, Celia Reig, Pilar Irún, Blanca Moreno, Pilar Giraldo, Jorge J. Cebolla

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Recommendations on the follow‐up of patients with Gaucher disease in Spain: Results from a Delphi survey by Pilar Giraldo, Marcio Andrade‐Campos, Montserrat Morales, the SEGA (SEguimiento del paciente de GAucher, Gaucher patient follow‐up) Group

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Critical review of clinical data and expert-based recommendations for the use of bosutinib in the treatment of chronic myeloid leukemia by Valentín García-Gutiérrez, María Teresa Gómez-Casares, Blanca Xicoy, Felipe Casado-Montero, Guillermo Orti, Pilar Giraldo, Juan Carlos Hernández-Boluda

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Evaluation of Lyso-Gb1 as a biomarker for Gaucher disease treatment outcomes using data from the Gaucher Outcome Survey by Ari Zimran, Shoshana Revel-Vilk, Tama Dinur, Majdolen Istaiti, Jaco Botha, Elena Lukina, Pilar Giraldo, Patrick Deegan, Stephan vom Dahl

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Muscle-tendon weakness contributes to chronic fatigue syndrome in Gaucher’s disease by Mercedes Roca-Espiau, Marcio Andrade-Campos, Jorge J. Cebolla, Laura López de Frutos, Blanca Medrano-Engay, Maria-Pilar López-Royo, Pilar Giraldo

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Aspectos clínicos, bioquímicos, moleculares y tratamiento de 2 pacientes con enfermedad de Gaucher Clinical, biochemical and molecular features and the treatment of two patients pr... by Kalia Lavaut Sánchez, Aramís Núñez Quintana, Ileana Nordet Carreras, Alejandro González Otero, Eva Svarch, Sergio Machín García, Pilar Giraldo, Clara Sá Miranda

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Real-world clinical experience with long-term miglustat maintenance therapy in type 1 Gaucher disease: the ZAGAL project by Pilar Giraldo, Pilar Alfonso, Koldo Atutxa, María A. Fernández-Galán, Abelardo Barez, Rafael Franco, Dora Alonso, Alejandro Martin, Paz Latre, Miguel Pocovi

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P1651: IMPACT OF NEUTROPHIL EXTRACELLULAR TRAPS (NETS) AND MACROPHAGE ACTIVATION IN THE THROMBOTIC EVENTS IN COVID-19 PATIENTS by Irene Serrano-Gonzalo, Bárbara Menéndez-Jandula, Isidro Arévalo-Vargas, Ester Franco-García, Carlos Lahoz, Paz Latre, Laura López de Frutos, Ralf Köhler, Pilar Giraldo

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Myelodysplasia-associated immunophenotypic alterations of bone marrow cells in myeloma: are they present at diagnosis or are they induced by lenalidomide? by Sergio Matarraz, Bruno Paiva, María Diez-Campelo, Lucia-López Corral, Estefanía Pérez, Maria-Victoria Mateos, Pilar Giraldo, Miguel T. Hernández, Jesús F. San Miguel, Alberto Orfao

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PB2198: TRIAL IN PROGRESS: AN OPEN-LABEL, GLOBAL, MULTICENTER, PHASE 1B/2 STUDY OF TL-895, A BRUTON’S TYROSINE KINASE INHIBITOR (BTKI), ADDED TO RUXOLITINIB (RUX) IN PATIENTS (PTS)... by Francesca Palandri, Stefanie Gröpper, Michael Loschi, Marcelo Bellesso, Sebastian Grosicki, Pilar Giraldo, Claire Harrison, Tracy Clevenger, Nikki Stuart, Hope Qamoos, Gregory Vosganian, Wayne P. Rothbaum, Srdan Verstovsek, Pankit Vachhani

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Safety and efficacy of pegunigalsidase alfa in patients with Fabry disease who were previously treated with agalsidase alfa: results from BRIDGE, a phase 3 open-label study by Aleš Linhart, Gabriela Dostálová, Kathy Nicholls, Michael L. West, Camilla Tøndel, Ana Jovanovic, Pilar Giraldo, Bojan Vujkovac, Tarekegn Geberhiwot, Einat Brill-Almon, Sari Alon, Raul Chertkoff, Rossana Rocco, Derralynn Hughes

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Identification of risk features for complication in Gaucher’s disease patients: a machine learning analysis of the Spanish registry of Gaucher disease by Marcio M. Andrade-Campos, Laura López de Frutos, Jorge J. Cebolla, Irene Serrano-Gonzalo, Blanca Medrano-Engay, Mercedes Roca-Espiau, Beatriz Gomez-Barrera, Jorge Pérez-Heredia, David Iniguez, Pilar Giraldo

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The effect of SARS-CoV-2 variant on respiratory features and mortality by Thomas D. Hughes, Ajan Subramanian, Rana Chakraborty, Shannon A. Cotton, Maria Del Pilar Giraldo Herrera, Yong Huang, Natalie Lambert, Melissa D. Pinto, Amir M. Rahmani, Carmen Josefa Sierra, Charles A. Downs

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The relevance of preferentially expressed antigen of melanoma (PRAME) as a marker of disease activity and prognosis in acute promyelocytic leukemia by Carlos Santamaría, María Carmen Chillón, Ramón García-Sanz, Ana Balanzategui, María Eugenia Sarasquete, Miguel Alcoceba, Fernando Ramos, Teresa Bernal, José Antonio Queizán, María Jesús Peñarrubia, Pilar Giraldo, Jesús F. San Miguel, Marcos Gonzalez

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Gpnmb Is a Potential Marker for the Visceral Pathology in Niemann-Pick Type C Disease. by André R A Marques, Tanit L Gabriel, Jan Aten, Cindy P A A van Roomen, Roelof Ottenhoff, Nike Claessen, Pilar Alfonso, Pilar Irún, Pilar Giraldo, Johannes M F G Aerts, Marco van Eijk

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