Emptying the stores: lysosomal diseases and therapeutic strategies by Platt, F

Substrate deprivation: a new therapeutic approach for the glycosphingolipid lysosomal storage diseases. by Platt, F, Butters, T

Miglustat - A viewpoint by Platt, F, Butters, T

Substrate reduction therapy by Platt, F, Butters, T

The metabolism of glucocerebrosides - From 1965 to the present. by Futerman, A, Platt, F

Introduction: Glycosphingolipids in cell biology and disease. by Sillence, D, Platt, F

An anecdotal report by an Oxford basic neuroscientist: effects of acetyl-dl-leucine on cognitive function and mobility in the elderly by Platt, F, Strupp, M

A new surrogate marker for CNS pathology in Niemann-Pick disease type C? by Platt, F, Lachmann, R

Substrate reduction therapy for glycosphingolipid storage disorders. by Lachmann, R, Platt, F

Treating lysosomal storage disorders: current practice and future prospects. by Platt, F, Lachmann, R

Glycosphingolipids in endocytic membrane transport. by Sillence, D, Platt, F

Substrate reduction therapy. by Platt, F, Jeyakumar, M

Storage diseases: new insights into sphingolipid functions. by Sillence, D, Platt, F

Lipids on trial: the search for the offending metabolite in Niemann-Pick type C disease. by Lloyd-Evans, E, Platt, F

Iminosugar inhibitors for treating the lysosomal glycosphingolipidoses by Butters, T, Dwek, R, Platt, F

Therapeutic applications of imino sugars in lysosomal storage disorders. by Butters, T, Dwek, R, Platt, F

Inhibition of glycosphingolipid biosynthesis: application to lysosomal storage disorders. by Butters, T, Dwek, R, Platt, F

Lysosomal Ca(2+) homeostasis: role in pathogenesis of lysosomal storage diseases. by Lloyd-Evans, E, Platt, F

Imino sugar inhibitors for treating the lysosomal glycosphingolipidoses. by Butters, T, Dwek, R, Platt, F

New therapeutics for the treatment of glycosphingolipid lysosomal storage diseases. by Butters, T, Dwek, R, Platt, F