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Results of a phase 1/2 study of cemdisiran in healthy subjects and patients with paroxysmal nocturnal hemoglobinuria by Anna Gaya, Talha Munir, Alvaro Urbano‐Ispizua, Morag Griffin, Jorg Taubel, Jim Bush, Ishir Bhan, Anna Borodovsky, Yue Wang, Prajakta Badri, Pushkal Garg
Published 2023-08-01
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Patisiran, an RNAi therapeutic for hereditary transthyretin-mediated amyloidosis: Sub-analysis in Taiwanese patients from the APOLLO study by Kon-Ping Lin, Chih-Chao Yang, Yi-Chung Lee, Ming-Jen Lee, John Vest, Marianne T. Sweetser, Matthew T. White, Prajakta Badri, Sung-Tsang Hsieh, Chi-Chao Chao
Published 2024-09-01
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