Adeno-Associated Virus Vectors for Therapeutic Gene Transfer by Jackie L. Stilwell, R. Jude Samulski

Get full text

Rationally engineered novel AAV capsids for intra-articular gene delivery by Wenjun Li, Susi Liu Feng, Lizette Herrschaft, R. Jude Samulski, Chengwen Li

Get full text

Corrigendum: Gene therapy approaches for equine osteoarthritis by Parvathy Thampi, R. Jude Samulski, Joshua C. Grieger, Jennifer N. Phillips, C. Wayne McIlwraith, Laurie R. Goodrich

Get full text

Gene therapy approaches for equine osteoarthritis by Parvathy Thampi, R. Jude Samulski, Joshua C. Grieger, Jennifer N. Phillips, C. Wayne McIlwraith, Laurie R. Goodrich

Get full text

AAV exploits subcellular stress associated with inflammation, endoplasmic reticulum expansion, and misfolded proteins in models of cystic fibrosis. by Jarrod S Johnson, Martina Gentzsch, Liqun Zhang, Carla M P Ribeiro, Boris Kantor, Tal Kafri, Raymond J Pickles, R Jude Samulski

Get full text

Thermostability and in vivo performance of AAV9 in a film matrix by Trang Nguyen Kieu Doan, Matthew D. Le, Irnela Bajrovic, Lorne Celentano, Charles Krause, Haley Grooms Balyan, Abbie Svancarek, Angela Mote, Anna Tretiakova, R. Jude Samulski, Maria A. Croyle

Get full text

Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity by Xiaolei Pei, Wenwei Shao, Allene Xing, Charles Askew, Xiaojing Chen, Caibin Cui, Yasmina L. Abajas, David A. Gerber, Elizabeth P. Merricks, Timothy C. Nichols, Wuping Li, R. Jude Samulski, Chengwen Li

Get full text

Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy by Caroline Le Guiner, Xiao Xiao, Thibaut Larcher, Aude Lafoux, Corinne Huchet, Gilles Toumaniantz, Oumeya Adjali, Ignacio Anegon, Séverine Remy, Josh Grieger, Juan Li, Vahid Farrokhi, Hendrik Neubert, Jane Owens, Maritza McIntyre, Philippe Moullier, R. Jude Samulski

Get full text