Quantitative analysis of α-L-iduronidase expression in immunocompetent mice treated with the Sleeping Beauty transposon system. by Elena L Aronovich, Bryan C Hall, Jason B Bell, R Scott McIvor, Perry B Hackett

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A Broad Range of Dose Optima Achieve High-level, Long-term Gene Expression After Hydrodynamic Delivery of Sleeping Beauty Transposons Using Hyperactive SB100x Transposase by Kelly M Podetz-Pedersen, Erik R Olson, Nikunj V Somia, Stephen J Russell, R Scott McIvor

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Differences in MPS I and MPS II Disease Manifestations by Christiane S. Hampe, Brianna D. Yund, Paul J. Orchard, Troy C. Lund, Jacob Wesley, R. Scott McIvor

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Mucopolysaccharidosis Type I: A Review of the Natural History and Molecular Pathology by Christiane S. Hampe, Julie B. Eisengart, Troy C. Lund, Paul J. Orchard, Monika Swietlicka, Jacob Wesley, R. Scott McIvor

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Non-invasive intravenous administration of AAV9 transducing iduronate sulfatase leads to global metabolic correction and prevention of neurologic deficits in a mouse model of Hunte... by Kanut Laoharawee, Kelly M. Podetz-Pedersen, Tam T. Nguyen, Sajya M. Singh, Miles C. Smith, Lalitha R. Belur, Walter C. Low, Karen F. Kozarsky, R. Scott McIvor

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Mucopolysaccharidosis Type I: Current Treatments, Limitations, and Prospects for Improvement by Christiane S. Hampe, Jacob Wesley, Troy C. Lund, Paul J. Orchard, Lynda E. Polgreen, Julie B. Eisengart, Linda K. McLoon, Sebahattin Cureoglu, Patricia Schachern, R. Scott McIvor

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Harnessing a high cargo-capacity transposon for genetic applications in vertebrates. by Darius Balciunas, Kirk J Wangensteen, Andrew Wilber, Jason Bell, Aron Geurts, Sridhar Sivasubbu, Xin Wang, Perry B Hackett, David A Largaespada, R Scott McIvor, Stephen C Ekker

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Comparative dose effectiveness of intravenous and intrathecal AAV9.CB7.hIDS, RGX-121, in mucopolysaccharidosis type II mice by Miles C. Smith, Lalitha R. Belur, Andrea D. Karlen, Olivia Erlanson, Justin Furcich, Troy C. Lund, Davis Seelig, Kelley F. Kitto, Carolyn A. Fairbanks, Kwi Hye Kim, Nick Buss, R. Scott McIvor

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Simple and efficient methods for enrichment and isolation of endonuclease modified cells. by Branden S Moriarity, Eric P Rahrmann, Dominic A Beckmann, Caitlin B Conboy, Adrienne L Watson, Daniel F Carlson, Erik R Olson, Kendra A Hyland, Scott C Fahrenkrug, R Scott McIvor, David A Largaespada

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Supraspinal gene transfer by intrathecal adeno-associated virus serotype 5 by Daniel J. Schuster, Lalitha R. Belur, Maureen S. Riedl, Stephen A. Schnell, Kelly M. Podetz-Pedersen, Kelley F. Kitto, R. Scott McIvor, Lucy eVulchanova, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Carolyn A. Fairbanks

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AAV-mediated gene transfer to colon-innervating primary afferent neurons by Reshma Gore, Tina Esmail, Kelsey Pflepsen, Ezequiel Marron Fernandez de Velasco, Kelley F. Kitto, Maureen S. Riedl, Andrea Karlen, R. Scott McIvor, Christopher N. Honda, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Lucy Vulchanova

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Adeno-associated virus-mediated gene transfer of arginine decarboxylase to the central nervous system prevents opioid analgesic tolerance by Caroline C. Churchill, Cristina D. Peterson, Cristina D. Peterson, Cristina D. Peterson, Kelley F. Kitto, Kelsey R. Pflepsen, Lalitha R. Belur, R. Scott McIvor, Lucy Vulchanova, George L. Wilcox, George L. Wilcox, George L. Wilcox, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Carolyn A. Fairbanks

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Correction of Fanconi Anemia Mutations Using Digital Genome Engineering by Christopher J. Sipe, Mitchell G. Kluesner, Samuel P. Bingea, Walker S. Lahr, Aneesha A. Andrew, Minjing Wang, Anthony P. DeFeo, Timothy L. Hinkel, Kanut Laoharawee, John E. Wagner, Margaret L. MacMillan, Gregory M. Vercellotti, Jakub Tolar, Mark J. Osborn, R. Scott McIvor, Beau R. Webber, Branden S. Moriarity

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333 Targeting the apical intracellular checkpoint CISH unleashes T cell neoantigen reactivity and effector program by Matthew Johnson, Ying Hu, Nicholas Restifo, Jared Gartner, Douglas Palmer, Shashank Patel, Maria Parkhurst, Todd Prickett, Parisa Malekzadeh, David McKenna, Zulmarie Franco, Suman Vodnala, Beau Webber, Yogin Patel, Christine Kariya, Walker Lahr, Rigel Kishton, Devikala Gurusamy, Miechaleen Diers, Natalie Wolf, Nicholas Slipek, Darin Sumstad, Lydia Viney, Tom Henley, Tilmann Bürckstümmer, Oliver Baker, Chunhua Yan, Daoud Meerzaman, Kartik Padhan, Winnie Lo, Li Jia, Drew Deniger, R Scott McIvor, Modassir Choudhry, Branden Moriarity