The Scope of Pathogenic ABCA4 Mutations Targetable by CRISPR DNA Base Editing Systems—A Systematic Review by Elena Piotter, Michelle E. McClements, Robert E. MacLaren, Robert E. MacLaren

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Comment on Di Giosaffatte et al. A Novel Hypothesis on Choroideremia-Manifesting Female Carriers: Could <i>CHM</i> In-Frame Variants Exert a Dominant Negative Effect? A Case Report... by Lewis E. Fry, Robert E. MacLaren

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Optogenetic Gene Therapy for the Degenerate Retina: Recent Advances by Michelle E. McClements, Federica Staurenghi, Robert E. MacLaren, Robert E. MacLaren, Jasmina Cehajic-Kapetanovic, Jasmina Cehajic-Kapetanovic

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Programmable RNA editing with endogenous ADAR enzymes – a feasible option for the treatment of inherited retinal disease? by Julia-Sophia Bellingrath, Michelle E. McClements, M. Dominik Fischer, M. Dominik Fischer, Robert E. MacLaren, Robert E. MacLaren

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Current and Future Landscape in Genetic Therapies for Leber Hereditary Optic Neuropathy by Hoda Shamsnajafabadi, Robert E. MacLaren, Jasmina Cehajic-Kapetanovic

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A Review of CRISPR Tools for Treating Usher Syndrome: Applicability, Safety, Efficiency, and In Vivo Delivery by Lauren Major, Michelle E. McClements, Robert E. MacLaren

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CRISPR-Cas9 DNA Base-Editing and Prime-Editing by Ariel Kantor, Michelle E. McClements, Robert E. MacLaren

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New CRISPR Tools to Correct Pathogenic Mutations in Usher Syndrome by Lauren Major, Michelle E. McClements, Robert E. MacLaren

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CRISPR Manipulation of Age-Related Macular Degeneration Haplotypes in the Complement System: Potential Future Therapeutic Applications/Avenues by Ahmed Salman, Michelle E. McClements, Robert E. MacLaren

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Therapy Approaches for Stargardt Disease by Elena Piotter, Michelle E McClements, Robert E MacLaren

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Insights on the Regeneration Potential of Müller Glia in the Mammalian Retina by Ahmed Salman, Michelle E. McClements, Robert E. MacLaren

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CRISPR DNA Base Editing Strategies for Treating Retinitis Pigmentosa Caused by Mutations in <i>Rhodopsin</i> by Maria Kaukonen, Michelle E. McClements, Robert E. MacLaren

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Minicircle Delivery to the Neural Retina as a Gene Therapy Approach by Federica Staurenghi, Michelle E. McClements, Ahmed Salman, Robert E. MacLaren

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Future Perspectives of Prime Editing for the Treatment of Inherited Retinal Diseases by Silja Hansen, Michelle E. McClements, Thomas J. Corydon, Robert E. MacLaren

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A cross-sectional study to assess the clinical utility of modern visual function assessments in patients with inherited retinal disease: a mixed methods observational study protoco... by Laura J. Taylor, Amandeep S. Josan, Irene Stratton, Jasleen K. Jolly, Robert E. MacLaren

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Accurate Quantification of AAV Vector Genomes by Quantitative PCR by Cristina Martinez-Fernandez de la Camara, Michelle E. McClements, Robert E. MacLaren

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CRISPR Interference–Potential Application in Retinal Disease by Caroline F. Peddle, Lewis E. Fry, Michelle E. McClements, Robert E. MacLaren

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Compound dominant-null heterozygosity in a family with RP1-related retinal dystrophy by Thomas M.W. Buckley, Jasmina Cehajic-Kapetanovic, Morag Shanks, Penny Clouston, Robert E. MacLaren

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The Biological Activity of AAV Vectors for Choroideremia Gene Therapy Can Be Measured by In Vitro Prenylation of RAB6A by Maria I. Patrício, Alun R. Barnard, Christopher I. Cox, Clare Blue, Robert E. MacLaren

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Non-Viral Delivery of CRISPR/Cas Cargo to the Retina Using Nanoparticles: Current Possibilities, Challenges, and Limitations by Ahmed Salman, Ariel Kantor, Michelle E. McClements, Gemma Marfany, Sonia Trigueros, Robert E. MacLaren

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