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Enhancing hemophilia A gene therapy by strategic F8 deletions in AAV vectors by Juan-Juan Zhao, Sai-Ning Tian, Xiang Li, Zu-Yi Peng, Guo-Hua Li, Feng Zhang, Mei Zhao, Jian-Ping Zhang, Xiao-Bing Zhang
Published 2025-01-01
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Decoding the complexity of on-target integration: characterizing DNA insertions at the CRISPR-Cas9 targeted locus using nanopore sequencing by Juan-Juan Zhao, Xin-Yu Sun, Sai-Ning Tian, Zong-Ze Zhao, Meng-Di Yin, Mei Zhao, Feng Zhang, Si-Ang Li, Zhi-Xue Yang, Wei Wen, Tao Cheng, An Gong, Jian-Ping Zhang, Xiao-Bing Zhang
Published 2024-02-01
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