Small GTPases Rab8a and Rab11a Are Dispensable for Rhodopsin Transport in Mouse Photoreceptors. by Guoxin Ying, Cecilia D Gerstner, Jeanne M Frederick, Sanford L Boye, William W Hauswirth, Wolfgang Baehr

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Inhibitor of apoptosis-stimulating protein of p53 (iASPP) is required for neuronal survival after axonal injury. by Ariel M Wilson, Vince A Chiodo, Sanford L Boye, Nicholas C Brecha, William W Hauswirth, Adriana Di Polo

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Evaluation of lateral spread of transgene expression following subretinal AAV-mediated gene delivery in dogs. by Ashlee R Bruewer, Freya M Mowat, Joshua T Bartoe, Sanford L Boye, William W Hauswirth, Simon M Petersen-Jones

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Capsid Mutated Adeno-Associated Virus Delivered to the Anterior Chamber Results in Efficient Transduction of Trabecular Meshwork in Mouse and Rat. by Barbara Bogner, Sanford L Boye, Seok Hong Min, James J Peterson, Qing Ruan, Zhonghong Zhang, Herbert A Reitsamer, William W Hauswirth, Shannon E Boye

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Recombinant AAV-mediated BEST1 transfer to the retinal pigment epithelium: analysis of serotype-dependent retinal effects. by Karina E Guziewicz, Barbara Zangerl, András M Komáromy, Simone Iwabe, Vincent A Chiodo, Sanford L Boye, William W Hauswirth, William A Beltran, Gustavo D Aguirre

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Development of an AAV-CRISPR-Cas9-based treatment for dominant cone-rod dystrophy 6 by Russell W. Mellen, Kaitlyn R. Calabro, K. Tyler McCullough, Sean M. Crosson, Alejandro de la Cova, Diego Fajardo, Emily Xu, Sanford L. Boye, Shannon E. Boye

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Novel Methodology for Creating Macaque Retinas with Sortable Photoreceptors and Ganglion Cells by Shreyasi Choudhury, Christianne E Strang, John J. Alexander, Miranda L. Scalabrino, Julie Lynch Hill, Daniel T. Kasuga, C. Douglas Witherspoon, Sanford L. Boye, Paul D. Gamlin, Shannon Elizabeth Boye

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Rationally Engineered AAV Capsids Improve Transduction and Volumetric Spread in the CNS by Nicholas M. Kanaan, Rhyomi C. Sellnow, Sanford L. Boye, Ben Coberly, Antonette Bennett, Mavis Agbandje-McKenna, Caryl E. Sortwell, William W. Hauswirth, Shannon E. Boye, Fredric P. Manfredsson

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Ab-externo AAV-mediated gene delivery to the suprachoroidal space using a 250 micron flexible microcatheter. by Marc C Peden, Jeff Min, Craig Meyers, Zachary Lukowski, Qiuhong Li, Sanford L Boye, Monica Levine, William W Hauswirth, Ramakrishna Ratnakaram, William Dawson, Wesley C Smith, Mark B Sherwood

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A Novel Mouse Model of MYO7A USH1B Reveals Auditory and Visual System Haploinsufficiencies by Kaitlyn R. Calabro, Sanford L. Boye, Shreyasi Choudhury, Diego Fajardo, James J. Peterson, Wei Li, Sean M. Crosson, Mi-Jung Kim, Dalian Ding, Richard Salvi, Shinichi Someya, Shannon E. Boye

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Gene Therapy in a Large Animal Model of PDE6A-Retinitis Pigmentosa by Freya M. Mowat, Freya M. Mowat, Laurence M. Occelli, Joshua T. Bartoe, Kristen J. Gervais, Ashlee R. Bruewer, Janice Querubin, Astra Dinculescu, Sanford L. Boye, William W. Hauswirth, Simon M. Petersen-Jones

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SARM1 depletion rescues NMNAT1-dependent photoreceptor cell death and retinal degeneration by Yo Sasaki, Hiroki Kakita, Shunsuke Kubota, Abdoulaye Sene, Tae Jun Lee, Norimitsu Ban, Zhenyu Dong, Joseph B Lin, Sanford L Boye, Aaron DiAntonio, Shannon E Boye, Rajendra S Apte, Jeffrey Milbrandt

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Gene-based Therapy in a Mouse Model of Blue Cone Monochromacy by Yuxin Zhang, Wen-Tao Deng, Wei Du, Ping Zhu, Jie Li, Fan Xu, Jingfen Sun, Cecilia D. Gerstner, Wolfgang Baehr, Sanford L. Boye, Chen Zhao, William W. Hauswirth, Ji-jing Pang

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Preclinical studies in support of phase I/II clinical trials to treat GUCY2D-associated Leber congenital amaurosis by Sanford L. Boye, Catherine O’Riordan, James Morris, Michael Lukason, David Compton, Rena Baek, Dana M. Elmore, James.J. Peterson, Diego Fajardo, K. Tyler McCullough, Abraham Scaria, Alison McVie-Wylie, Shannon E. Boye

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Safety and improved efficacy signals following gene therapy in childhood blindness caused by GUCY2D mutations by Samuel G. Jacobson, Artur V. Cideciyan, Allen C. Ho, Igor V. Peshenko, Alexandra V. Garafalo, Alejandro J. Roman, Alexander Sumaroka, Vivian Wu, Arun K. Krishnan, Rebecca Sheplock, Sanford L. Boye, Alexander M. Dizhoor, Shannon E. Boye

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Dual-AAV vector-mediated expression of MYO7A improves vestibular function in a mouse model of Usher syndrome 1B by Samantha C. Lau, Mhamed Grati, Kevin Isgrig, Moaz Sinan, Kaitlyn R. Calabro, Jianliang Zhu, Yasuko Ishibashi, Zeynep Ozgur, Talah Wafa, Inna A. Belyantseva, Tracy Fitzgerald, Thomas B. Friedman, Sanford L. Boye, Shannon E. Boye, Wade W. Chien

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AAV-mediated cone rescue in a naturally occurring mouse model of CNGA3-achromatopsia. by Ji-jing Pang, Wen-Tao Deng, Xufeng Dai, Bo Lei, Drew Everhart, Yumiko Umino, Jie Li, Keqing Zhang, Song Mao, Sanford L Boye, Li Liu, Vince A Chiodo, Xuan Liu, Wei Shi, Ye Tao, Bo Chang, William W Hauswirth

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Correction: AAV-Mediated Cone Rescue in a Naturally Occurring Mouse Model of CNGA3-Achromatopsia. by Ji-jing Pang, Wen-Tao Deng, Xufeng Dai, Bo Lei, Drew Everhart, Yumiko Umino, Jie Li, Keqing Zhang, Song Mao, Sanford L. Boye, Li Liu, Vince A. Chiodo, Xuan Liu, Wei Shi, Ye Tao, Bo Chang, William W. Hauswirth

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Correction: Targeting Photoreceptors via Intravitreal Delivery Using Novel, Capsid-Mutated AAV Vectors. by Christine N. Kay, Renee C. Ryals, George V. Aslanidi, Seok Hong Min, Qing Ruan, Jingfen Sun, Frank M. Dyka, Daniel Kasuga, Andrea E. Ayala, Kim Van Vliet, Mavis Agbandje-McKenna, William W. Hauswirth, Sanford L. Boye, Shannon E. Boye

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Adeno-Associated Virus (AAV) Capsid Stability and Liposome Remodeling During Endo/Lysosomal pH Trafficking by Bridget Lins-Austin, Saajan Patel, Mario Mietzsch, Dewey Brooke, Antonette Bennett, Balasubramanian Venkatakrishnan, Kim Van Vliet, Adam N. Smith, Joanna R. Long, Robert McKenna, Mark Potter, Barry Byrne, Sanford L. Boye, Brian Bothner, Regine Heilbronn, Mavis Agbandje-McKenna

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