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Pozelimab for CHAPLE disease: results from in-trial interviews and clinical outcome assessments by Leighann Litcher-Kelly, Ahmet Ozen, Sarah Ollis, Hagit Baris Feldman, Andrew Yaworsky, Paolo Medrano, Voranush Chongsrisawa, Taylor Brackin, Lorah Perlee, Marisa Walker, Sharanya Pradeep, Michael J. Lenardo, Olivier A. Harari, Jessica J. Jalbert
Published 2024-08-01
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The patient experience of CHAPLE disease: results from interviews conducted as part of a clinical trial for an ultra-rare condition by Leighann Litcher-Kelly, Ahmet Ozen, Sarah Ollis, Hagit Baris Feldman, Andrew Yaworsky, Paolo Medrano, Voranush Chongsrisawat, Lorah Perlee, Marisa Walker, Sharanya Pradeep, Diane M. Turner-Bowker, Alina Kurolap, Orly Eshach Adiv, Michael J. Lenardo, Olivier A. Harari, Jessica J. Jalbert
Published 2025-02-01
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