Retinal pigment epithelium defects accelerate photoreceptor degeneration in cell type-specific knockout mouse models of choroideremia. за авторством Tolmachova, T, Wavre-Shapton, S, Barnard, A, Maclaren, R, Futter, C, Seabra, M

AAV2/2-CBA-REP1 Vector with WPRE Provides Functional Expression of the Transgene in Choroideremia Mouse Knock-Out and Patient Cells за авторством Tolmachova, T, Tolmachov, O, Barnard, A, Groppe, M, During, M, MacLaren, R, Seabra, M

Functional expression of Rab escort protein 1 following AAV2-mediated gene delivery in the retina of choroideremia mice and human cells ex vivo. за авторством Tolmachova, T, Tolmachov, O, Barnard, A, Silva, D, Lipinski, D, Walker, N, Maclaren, R, Seabra, M

Functional expression of Rab escort protein 1 following AAV2-mediated gene delivery in the retina of choroideremia mice and human cells ex vivo за авторством Tolmachova, T, Tolmachov, O, Barnard, A, Silva, D, Lipinski, D, Walker, N, MacLaren, R, Seabra, M

Retinal gene therapy in patients with choroideremia: Initial fi ndings from a phase 1/2 clinical trial за авторством MacLaren, R, MacLaren, R, MacLaren, R, Groppe, M, Groppe, M, Groppe, M, Barnard, A, Cottriall, C, Tolmachova, T, Seymour, L, Reed Clark, K, During, M, Cremers, F, Black, G, Lotery, A, Downes, S, Downes, S, Webster, A, Webster, A, Seabra, M, Seabra, M

Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial. за авторством Maclaren, R, Groppe, M, Barnard, A, Cottriall, C, Tolmachova, T, Seymour, L, Clark, K, During, M, Cremers, F, Black, G, Lotery, A, Downes, S, Webster, A, Seabra, M

Visual acuity after retinal gene therapy for Choroideremia за авторством Edwards, T, Jolly, J, Groppe, M, Barnard, A, Cottriall, C, Tolmachova, T, Black, G, Webster, A, Lotery, A, Holder, G, Xue, K, Downes, S, Simunovic, M, Seabra, M, MacLaren, R

Beneficial effects on vision in patients undergoing retinal gene therapy for choroideremia за авторством Xue, K, Jolly, J, Barnard, A, Rudenko, A, Salvetti, A, Patrício, M, Edwards, T, Groppe, M, Orlans, H, Tolmachova, T, Black, G, Webster, A, Lotery, A, Holder, G, Downes, S, Seabra, M, MacLaren, R

Synthesis, chiral high performance liquid chromatographic resolution and enantiospecific activity of a potent new geranylgeranyl transferase inhibitor, 2-hydroxy-3-imidazo[1,2-a]py... за авторством McKenna, C, Kashemirov, B, Błazewska, K, Mallard-Favier, I, Stewart, C, Rojas, J, Lundy, M, Ebetino, F, Baron, R, Dunford, J, Kirsten, M, Seabra, M, Bala, J, Marma, MS, Rogers, M, Coxon, F