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Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model by Overby, SJ, Cerro-Herreros, E, González-Martínez, I, Varela, MA, Seoane-Miraz, D, Jad, Y, Raz, R, Møller, T, Pérez-Alonso, M, Wood, MJ, Llamusí, B, Artero, R
Published 2022Journal article -
2
Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy by Cerro-Herreros, E, González-Martínez, I, Moreno, N, Espinosa-Espinosa, J, Fernández-Costa, JM, Colom-Rodrigo, A, Overby, SJ, Seoane-Miraz, D, Poyatos-García, J, Vilchez, JJ, López de Munain, A, Varela, MA, Wood, MJ, Pérez-Alonso, M, Llamusí, B, Artero, R
Published 2021Journal article -
3
TDP-43 regulates LC3ylation in neural tissue through ATG4B cryptic splicing inhibition by Torres, P, Rico-Rios, S, Ceron-Codorniu, M, Santacreu-Vilaseca, M, Seoane-Miraz, D, Jad, Y, Ayala, V, Mariño, G, Beltran, M, Miralles, MP, Andrés-Benito, P, Fernandez-Irigoyen, J, Santamaria, E, López-Otín, C, Soler, RM, Povedano, M, Ferrer, I, Pamplona, R, Wood, MJA, Varela, MA, Portero-Otin, M
Published 2024Journal article