Showing 1 - 7 results of 7 for search 'Shibi Likhite', query time: 0.31s
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A Novel Retinal Gene Therapy Strategy for Batten Disease and Beyond by Maura Schwartz, Alex Campbell, Joseph Caporale, Megan Baird, Isabella Palazzo, Shibi Likhite, Andrew Fischer, Kathrin Meyer
Published 2020-11-01
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In Vitro Modeling as a Tool for Testing Therapeutics for Spinal Muscular Atrophy and IGHMBP2-Related Disorders by Julieth Andrea Sierra-Delgado, Shrestha Sinha-Ray, Abuzar Kaleem, Meysam Ganjibakhsh, Mohini Parvate, Samantha Powers, Xiaojin Zhang, Shibi Likhite, Kathrin Meyer
Published 2023-06-01
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In-depth comparison of Anc80L65 and AAV9 retinal targeting and characterization of cross-reactivity to multiple AAV serotypes in humans by Maura K. Schwartz, Shibi Likhite, Tatyana A. Vetter, Megan C. Baird, Vicki McGovern, Andrea Sierra Delgado, Tom Mendel, Arthur Burghes, Kathrin C. Meyer
Published 2023-09-01
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Neurotoxic Astrocytes Directly Converted from Sporadic and Familial ALS Patient Fibroblasts Reveal Signature Diversities and miR-146a Theragnostic Potential in Specific Subtypes by Cátia Gomes, Catarina Sequeira, Shibi Likhite, Cassandra N. Dennys, Stephen J. Kolb, Pamela J. Shaw, Ana R. Vaz, Brian K. Kaspar, Kathrin Meyer, Dora Brites
Published 2022-04-01
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Prevalence of Neutralizing Antibodies against Adeno-Associated Virus Serotypes 1, 2, and 9 in Non-Injected Latin American Patients with Heart Failure—ANVIAS Study by Julieth A. Sierra-Delgado, Shibi Likhite, Paula K. Bautista, Sergio A. Gómez-Ochoa, Luis E. Echeverría, Elizabeth Guío, Clara Vargas, Norma C. Serrano, Kathrin C. Meyer, Melvin Y. Rincon
Published 2023-03-01
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Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease by Tyler B. Johnson, Tyler B. Johnson, Jon J. Brudvig, Jon J. Brudvig, Shibi Likhite, Melissa A. Pratt, Katherine A. White, Jacob T. Cain, Jacob T. Cain, Clarissa D. Booth, Derek J. Timm, Samantha S. Davis, Brandon Meyerink, Ricardo Pineda, Cassandra Dennys-Rivers, Brian K. Kaspar, Kathrin Meyer, Jill M. Weimer, Jill M. Weimer, Jill M. Weimer
Published 2023-03-01
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