<i>LMNA</i> Co-Regulated Gene Expression as a Suitable Readout after Precise Gene Correction by Haicui Wang, Anne Krause, Helena Escobar, Stefanie Müthel, Eric Metzler, Simone Spuler

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mRNA-mediated delivery of gene editing tools to human primary muscle stem cells by Christian Stadelmann, Silvia Di Francescantonio, Andreas Marg, Stefanie Müthel, Simone Spuler, Helena Escobar

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Cas9-induced single cut enables highly efficient and template-free repair of a muscular dystrophy causing founder mutation by Stefanie Müthel, Andreas Marg, Busem Ignak, Janine Kieshauer, Helena Escobar, Christian Stadelmann, Simone Spuler

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Base editing repairs an SGCA mutation in human primary muscle stem cells by Helena Escobar, Anne Krause, Sandra Keiper, Janine Kieshauer, Stefanie Müthel, Manuel García de Paredes, Eric Metzler, Ralf Kühn, Florian Heyd, Simone Spuler

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Disintegration of the NuRD Complex in Primary Human Muscle Stem Cells in Critical Illness Myopathy by Joanna Schneider, Devakumar Sundaravinayagam, Alexander Blume, Andreas Marg, Stefanie Grunwald, Eric Metzler, Helena Escobar, Stefanie Müthel, Haicui Wang, Tobias Wollersheim, Steffen Weber-Carstens, Altuna Akalin, Michela Di Virgilio, Baris Tursun, Simone Spuler

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