Construction and Cloning of Minigenes for in vivo Analysis of Potential Splice Mutations by Lisa Riedmayr, Sybille Böhm, Stylianos Michalakis, Elvir Becirovic

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Antisense Oligonucleotide- and CRISPR-Cas9-Mediated Rescue of mRNA Splicing for a Deep Intronic CLRN1 Mutation by Anna-Lena Panagiotopoulos, Nina Karguth, Marina Pavlou, Sybille Böhm, Gilles Gasparoni, Jörn Walter, Alexander Graf, Helmut Blum, Martin Biel, Lisa Maria Riedmayr, Elvir Becirovic

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Peripherin-2 and Rom-1 have opposing effects on rod outer segment targeting of retinitis pigmentosa-linked peripherin-2 mutants by Sybille Böhm, Lisa M. Riedmayr, O. N. Phuong Nguyen, Andreas Gießl, Toni Liebscher, Elisabeth S. Butz, Christian Schön, Stylianos Michalakis, Christian Wahl-Schott, Martin Biel, Elvir Becirovic

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In Vivo Analysis of Disease-Associated Point Mutations Unveils Profound Differences in mRNA Splicing of Peripherin-2 in Rod and Cone Photoreceptors. by Elvir Becirovic, Sybille Böhm, Ong Nam Phuong Nguyen, Lisa Maria Riedmayr, Mirja Annika Koch, Elisabeth Schulze, Susanne Kohl, Oliver Borsch, Tiago Santos-Ferreira, Marius Ader, Stylianos Michalakis, Martin Biel

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mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapy by Lisa Maria Riedmayr, Klara Sonnie Hinrichsmeyer, Stefan Bernhard Thalhammer, David Manuel Mittas, Nina Karguth, Dina Yehia Otify, Sybille Böhm, Valentin Johannes Weber, Michael David Bartoschek, Victoria Splith, Manuela Brümmer, Raphael Ferreira, Nanda Boon, Gabriele Maria Wögenstein, Christian Grimm, Jan Wijnholds, Verena Mehlfeld, Stylianos Michalakis, Stefanie Fenske, Martin Biel, Elvir Becirovic

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