Showing 1 - 3 results of 3 for search 'T. M. Yiu', query time: 0.02s
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Long-term safety of dexamethasone sodium phosphate encapsulated in autologous erythrocytes in pediatric patients with ataxia telangiectasia by Mary Kay Koenig, Vincenzo Leuzzi, Riadh Gouider, Riadh Gouider, Eppie M. Yiu, Eppie M. Yiu, Barbara Pietrucha, Asbjørg Stray-Pedersen, Susan L. Perlman, Steve Wu, Trudy Burgers, Rupam Borgohain, Rukmini Mridula Kandadai, Isabelle Meyts, Giorgia Bucciol, Anaita Udwadia-Hegde, Ravi Yadav, Donna Roberts, Aaron Dane, Maureen Roden, Dirk Thye, Biljana Horn, Howard M. Lederman, William P. Whitehouse
Published 2025-01-01
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A contemporary analysis of the Australian clinical and genetic landscape of spinal muscular atrophy: a registry based studyResearch in context by Lakshmi Balaji, Robin Forbes, Anita Cairns, Hugo Sampaio, Andrew J. Kornberg, Lauren Sanders, Phillipa Lamont, Christina Liang, Kristi J. Jones, Kristen Nowak, Cullen O'Gorman, Ian Woodcock, Nancy Briggs, Eppie M. Yiu, Michelle A. Farrar, Didu Kariyawasam
Published 2024-12-01
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A phase 2 open-label study of the safety and efficacy of weekly dosing of ATL1102 in patients with non-ambulatory Duchenne muscular dystrophy and pharmacology in mdx mice by Ian R. Woodcock, George Tachas, Nuket Desem, Peter J. Houweling, Michael Kean, Jaiman Emmanuel, Rachel Kennedy, Kate Carroll, Katy de Valle, Justine Adams, Shireen R. Lamandé, Chantal Coles, Chrystal Tiong, Matthew Burton, Daniella Villano, Peter Button, Jean-Yves Hogrel, Sarah Catling-Seyffer, Monique M. Ryan, Martin B. Delatycki, Eppie M. Yiu
Published 2024-01-01
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