PB2345: ADAPTING PATIENT EDUCATIONAL APPROACHES IN PYRUVATE KINASE DEFICIENCY: EUROPE AND NORTH AMERICA FINDINGS FROM THE AAC PATIENT AND CAREGIVER SURVEY by W. Barcellini, R. Grace

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P1555: IRON CHELATION THERAPY IN CONGENITAL HEMOLYTIC ANEMIAS: AN ITALIAN SINGLE CENTER STUDY by A. Bosi, B. Fattizzo, J. A. Giannotta, I. Papetti, W. Barcellini

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P1533: TRIAL IN PROGRESS: A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED PHASE 3 STUDY OF THE EFFICACY AND SAFETY OF PARSACLISIB IN PATIENTS WITH PRIMARY WARM AUTOIMMUNE HEMOLYTIC... by W. Barcellini, K. Butler, S. Moran, K. Bibeau, I. Dzhindzhikhashvili, S. Wei, U. Jäger

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PB1935: MANAGEMENT OF NON-SEVERE APLASTIC ANEMIA: LABORATORY WORKUP AND TREATMENT PATTERNS. by G. Cassanello, J. A. Giannotta, L. Cro, M. Barbieri, W. Barcellini, B. Fattizzo

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P1526: AUTOIMMUNE HEMOLYTIC ANEMIAS: RELATIONSHIP BETWEEN SINGLE NUCLEOTIDE POLYMORPHISMS OF CYTOKINE GENES AND CLINICAL/HEMATOLOGICAL PARAMETERS by A. Zaninoni, B. Fattizzo, J. Giannotta, E. Fermo, P. Bianchi, N. Cecchi, W. Barcellini

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S286: LONG-TERM EFFICACY AND SAFETY RESULTS FROM AN ONGOING OPEN-LABEL PHASE 2 STUDY OF PARSACLISIB FOR THE TREATMENT OF AUTOIMMUNE HEMOLYTIC ANEMIA (AIHA) by W. Barcellini, I. Murakhovskaya, L. Terriou, F. Pane, A. Patriarca, K. Butler, S. Moran, S. Wei, U. Jäger

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P1725: OBSERVATIONAL STUDY TO EVALUATE PATIENT-REPORTED OUTCOMES IN PAROXYSMAL NOCTURNAL HEMOGLOBINURIA by E. Urciuoli, E. Di Bona, S. Greve, A. De Vivo, S. Sica, R. Fontana, W. Barcellini, L. Marano, E. N. Oliva

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P1735: IMPROVEMENTS IN PATIENT-REPORTED OUTCOMES IN MITAPIVAT-TREATED PATIENTS WITH PYRUVATE KINASE DEFICIENCY: A DESCRIPTIVE ANALYSIS FROM THE PHASE 3 ACTIVATE TRIAL by K. H. Kuo, R. F. Grace, E. J. van Beers, W. Barcellini, A. Glenthøj, S. Holzhauer, P. Patel, V. Beynon, J. Li, E. Zagadailov, H. Al-Samkari

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S278: EVALUATION OF THE MAIN REGULATORS OF SYSTEMIC IRON HOMEOSTASIS IN PYRUVATE KINASE DEFICIENCY by A. Zaninoni, R. Russo, R. Marra, I. Andolfo, E. Fermo, A. P. Marcello, D. Consonni, B. Eleni Rosato, S. Martone, B. Fattizzo, W. Barcellini, A. Iolascon, P. Bianchi

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S304: SUTIMLIMAB, A COMPLEMENT C1S INHIBITOR, PROVIDES SUSTAINED IMPROVEMENTS IN PATIENT-REPORTED OUTCOMES IN PATIENTS WITH COLD AGGLUTININ DISEASE (CAD): 2 YEAR FOLLOW-UP FROM THE... by A. Röth, C. M. Broome, W. Barcellini, T. Henrik Anderson Tvedt, Y. Miyakawa, S. D’Sa, D. Cella, F. Joly, J. Wang, T. Sourdille, F. Shafer, M. Wardęcki, I. C. Weitz

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SUTIMLIMAB, A COMPLEMENT C1S INHIBITOR, IMPROVES QUALITY OF LIFE IN PATIENTS WITH COLD AGGLUTININ DISEASE: PATIENT-REPORTED OUTCOMES RESULTS OF THE PHASE 3 CARDINAL STUDY by M.M.O. Barros, A. Röth, W. Barcellini, T.H.A. Tvedt, Y. Miyakawa, D.J. Kuter, W. Hobbs, J. Su, X. Jiang, J.M. Arias, I.C. Weitz

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P1565: MITAPIVAT IMPROVES INEFFECTIVE ERYTHROPOIESIS AND REDUCES IRON OVERLOAD IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY by E. J. van Beers, H. Al-Samkari, R. F. Grace, W. Barcellini, A. Glenthøj, M. P. Judge, P. A. Kosinski, R. Xu, V. Beynon, B. McGee, J. B. Porter, K. H. M. Kuo

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P1525: MANAGEMENT OF AUTOIMMUNE HAEMOLYTIC ANAEMIA DURING PREGNANCY OR POST-PARTUM: AN INTERNATIONAL MULTI-CENTRE EXPERIENCE. by M. Bortolotti, N. N. Fantini, A. Glenthoj, M. Michel, M. Napolitano, S. Raso, F. Chen, V. McDonald, I. Murakhovskaya, J. M. I. Vos, A. Patriarca, M. E. Mingot-Castellano, D. Prati, W. Barcellini, B. Fattizzo

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P1538: INHIBITION OF COMPLEMENT C1S WITH SUTIMLIMAB IN PATIENTS WITH COLD AGGLUTININ DISEASE (CAD): RESULTS FOLLOWING 9-WEEK WASHOUT PERIOD IN PHASE 3 CARDINAL STUDY (NCT03347396) by A. Röth, W. Barcellini, S. D’Sa, Y. Miyakawa, C. M. Broome, M. Michel, D. J. Kuter, B. Jilma, T. H. A. Tvedt, I. C. Weitz, T. Sourdille, J. Wang, D. S. Vagge, K. Kralova, F. Shafer, M. Wardecki, M. Lee, S. Berentsen

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S285: INHIBITION OF COMPLEMENT C1S WITH SUTIMLIMAB IN PATIENTS WITH COLD AGGLUTININ DISEASE (CAD): 2-YEAR FOLLOW-UP FROM THE CARDINAL STUDY by A. Röth, W. Barcellini, S. D’Sa, Y. Miyakawa, C. M. Broome, M. Michel, D. J. Kuter, B. Jilma, T. H. A. Tvedt, I. C. Weitz, T. Sourdille, J. Wang, D. S. Vagge, K. Kralova, F. Shafer, M. Wardecki, M. Lee, S. Berentsen

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P1548: LONG-TERM TREATMENT WITH ORAL MITAPIVAT IS ASSOCIATED WITH NORMALIZATION OF HEMOGLOBIN LEVELS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY by W. Barcellini, R. F. Grace, H. Al-Samkari, A. Glenthøj, J. A. Rothman, M. Morado Arias, D. M. Layton, O. Andres, M. DiBacco, P. Hawkins, M. P. Judge, F. Tai, J. Morales-Arias, V. Beynon, E. J. van Beers

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P1544: BONE MINERAL DENSITY REMAINS STABLE IN PYRUVATE KINASE DEFICIENCY PATIENTS RECEIVING LONG-TERM TREATMENT WITH MITAPIVAT by H. Al-Samkari, R. F. Grace, A. Glenthøj, O. Andres, W. Barcellini, F. Galactéros, K. H. M. Kuo, D. M. Layton, M. Morado Arias, V. Viprakasit, Y. Dong, F. Tai, L. Grekas, K. Khoja, S. Gheuens, B. McGee, J. B. Porter, E. J. van Beers

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P1545: DURABILITY OF HEMOGLOBIN RESPONSE AND REDUCTION IN TRANSFUSION BURDEN IS MAINTAINED OVER TIME IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY TREATED WITH MITAPIVAT IN A LONG-TE... by R. F. Grace, A. Glenthøj, W. Barcellini, M. Verhovsek, J. A. Rothman, M. Morado Arias, D. M. Layton, O. Andres, F. Galactéros, E. J. van Beers, K. Onodera, V. Viprakasit, S. Chonat, J. B. Porter, M. P. Judge, P. A. Kosinski, P. Hawkins, S. Gheuens, R. Xu, B. McGee, V. Beynon, H. Al-Samkari

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