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P173: Establishing preclinical efficacy for the first AAV gene therapy for GSD IX γ2 across stages of progressive liver disease by Rebecca Gibson, Jeong-A Lim, Su Jin Choi, Neha Jumani, Deeksha Bali, Sarah Young, William Jeck, Baodong Sun, Aravind Asokan, Priya Kishnani
Published 2023-01-01
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