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Evaluation of efficacy and safety of AAV8-ΔC4ATP7B gene therapy in a mutant mouse model of Wilson’s disease by Chunhua Zeng, Yunting Lin, Xinshuo Lu, Shehong Chen, Yan Xia, Kangdi Zhang, Yongxian Shao, Zhihong Guan, Rong Du, Zongcai Liu, Mingqi Zhao, Xiaoling Jiang, Yanna Cai, Taolin Li, Xueying Su, Yaoyong Chen, Xiaoyan Dong, Wen Zhang, Li Liu, Wenhao Zhou
Published 2025-03-01
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