Therapeutic strategies for spinal muscular atrophy: SMN and beyond nork Bowerman, M, Becker, C, Yáñez-Muñoz, R, Ning, K, Wood, M, Gillingwater, T, Talbot, K, UK SMA Research Consortium

Enhanced Efficacy of the CDNF/MANF Family by Combined Intranigral Overexpression in the 6-OHDA Rat Model of Parkinson's Disease. nork Cordero-Llana, O, Houghton, B, Rinaldi, F, Taylor, H, Yáñez-Muñoz, R, Uney, J, Wong, L, Caldwell, M

Therapeutic strategies for spinal muscular atrophy: SMN and beyond nork Bowerman, M, Becker, C, Yáñez-Muñoz, R, Ning, K, Wood, M, Gillingwater, T, Talbot, K, UK SMA Research Consortium

Gene Correction of a Duchenne Muscular Dystrophy Mutation by Meganuclease-Enhanced Exon Knock-In nork Popplewell, L, Koo, T, Leclerc, X, Duclert, A, Mamchaoui, K, Gouble, A, Mouly, V, Voit, T, Pâques, F, Cédrone, F, Isman, O, Yáñez-Muñoz, R, Dickson, G

Effective gene therapy with nonintegrating lentiviral vectors. nork Yáñez-Muñoz, R, Balaggan, K, MacNeil, A, Howe, S, Schmidt, M, Smith, A, Buch, P, Maclaren, R, Anderson, P, Barker, SE, Duran, Y, Bartholomae, C, von Kalle, C, Heckenlively, JR, Kinnon, C, Ali, R, Thrasher, A

Chromosomal context and epigenetic mechanisms control the efficacy of genome editing by rare-cutting designer endonucleases nork Daboussi, F, Zaslavskiy, M, Poirot, L, Loperfido, M, Gouble, A, Guyot, V, Leduc, S, Galetto, R, Grizot, S, Oficjalska, D, Perez, C, Delacote, F, Dupuy, A, Chion-Sotinel, I, Le Clerre, D, Lebuhotel, C, Danos, O, Lemaire, F, Oussedik, K, Cedrone, F, Epinat, J, Smith, J, Yanez-Munoz, R, Dickson, G, Popplewell, L