Experience of using gene replacement therapy with Zolgensma® (onasemnogene abeparvovec) in real clinical practice in Russia by S. B. Artemyeva, Yu. O. Papina, O. A. Shidlovskaya, A. V. Monakhova, D. V. Vlodavets

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Functional class criteria identification in patients with spinal muscular atrophy 5q by Yu. O. Papina, E. A. Melnik, E. D. Belousova, S. B. Artemyeva, A. V. Monakhova, O. A. Shidlovskaya, I. V. Shulyakova, D. V. Vlodavets

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Approaches to pathogenetic therapy of spinal muscular atrophy in children and newborns by S. B. Artemyeva, O. A. Shidlovskaya, Yu. O. Papina, A. V. Monakhova, I. V. Shulyakova, E. D. Belousova, O. Yu. Germanenko, D. V. Vlodavets

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The efficacy and safety of nusinersen within the expanded access program in Russia by S. B. Artemieva, L. M. Kuzenkova, E. S. Ilyina, Yu. A. Kursakova, L. M. Kolpakchi, E. Yu. Sapego, A. A. Golenko, S. G. Popovich, D. V. Parshin, O. A. Shidlovskaya, Yu. O. Papina, A. V. Monakhova, D. V. Vlodavets

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