RNA-Seq Analysis of Trans-Differentiated ARPE-19 Cells Transduced by AAV9-AIPL1 Vectors

RNA-Seq Analysis of Trans-Differentiated ARPE-19 Cells Transduced by AAV9-AIPL1 Vectors

Inherited retinal disorders (IRD) have become a primary focus of gene therapy research since the success of adeno-associated virus-based therapeutics (voretigene neparvovec-rzyl) for Leber congenital amaurosis type 2 (LCA2). Dozens of monogenic IRDs could be potentially treated with a similar approa...

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Bibliographic Details
Main Authors: Alima Galieva, Alexander Egorov, Alexander Malogolovkin, Andrew Brovin, Alexander Karabelsky
Format: Article
Language:English
Published: MDPI AG 2023-12-01
Series:International Journal of Molecular Sciences
Subjects:
AAV
AAV9
AIPL1
RNA-seq
ARPE-19
Leber congenital amaurosis
Online Access:https://www.mdpi.com/1422-0067/25/1/197

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