Minimal clinically important differences in six-minute walking distance in late-onset Pompe disease

Minimal clinically important differences in six-minute walking distance in late-onset Pompe disease

Abstract Background The minimal clinically important difference (MCID) is the smallest change in outcome that physicians or patients would consider meaningful and is relevant when evaluating disease progression or the efficacy of interventions. Studies of patients with late-onset Pompe disease (LOPD...

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Bibliographic Details
Main Authors: Kristl G. Claeys, Hani Kushlaf, Syed Raza, Noemi Hummel, Simon Shohet, Ian Keyzor, Agnieszka Kopiec, Ryan Graham, Brian Fox, Benedikt Schoser
Format: Article
Language:English
Published: BMC 2024-04-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Minimal clinically important difference
MCID
Six-minute walk distance
6MWD
Late-onset Pompe disease
Disease severity
Online Access:https://doi.org/10.1186/s13023-024-03156-3

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