Assessment of Activity of Daily Life in Mucopolysaccharidosis Type II Patients with Hematopoietic Stem Cell Transplantation

Assessment of Activity of Daily Life in Mucopolysaccharidosis Type II Patients with Hematopoietic Stem Cell Transplantation

The effectiveness of hematopoietic stem cell transplantation (HSCT) for mucopolysaccharidosis type II (MPS II, Hunter disease) remains controversial although recent studies have shown HSCT provides more clinical impact. This study aims to evaluate the long-term effectiveness of HSCT using the activi...

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Bibliographic Details
Main Authors:	Yasuyuki Suzuki, Madeleine Taylor, Kenji Orii, Toshiyuki Fukao, Tadao Orii, Shunji Tomatsu
Format:	Article
Language:	English
Published:	MDPI AG 2020-01-01
Series:	Diagnostics
Subjects:	mucopolysaccharidoses hunter syndrome activity of daily living hematopoietic stem cell transplantation
Online Access:	https://www.mdpi.com/2075-4418/10/1/46

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