The clinical course of Duchenne muscular dystrophy in the corticosteroid treatment era: a systematic literature review
Abstract Background Duchenne muscular dystrophy (DMD) is a severe rare progressive inherited neuromuscular disorder, leading to loss of ambulation (LOA) and premature mortality. The standard of care for patients with DMD has been treatment with corticosteroids for the past decade; however a synthesi...
Main Authors: | Shelagh M. Szabo, Renna M. Salhany, Alison Deighton, Meagan Harwood, Jean Mah, Katherine L. Gooch |
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Format: | Article |
Language: | English |
Published: |
BMC
2021-05-01
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Series: | Orphanet Journal of Rare Diseases |
Subjects: | |
Online Access: | https://doi.org/10.1186/s13023-021-01862-w |
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