Lysosomal Acid Lipase Deficiency: Therapeutic Options

Lysosomal Acid Lipase Deficiency: Therapeutic Options

Gregory M Pastores,1 Derralynn A Hughes2 1Department of Medicine (Genetics)/National Centre for Inherited Metabolic Disorders, Mater Misericordiae University Hospital and University College Dublin, Dublin, Ireland; 2Royal Free London NHS Foundation Trust, University College London, London NW3 2QG, U...

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Bibliographic Details
Main Authors:	Pastores GM, Hughes DA
Format:	Article
Language:	English
Published:	Dove Medical Press 2020-02-01
Series:	Drug Design, Development and Therapy
Subjects:	atherosclerosis dyslipidemia enzyme replacement therapy hepatomegaly lipid-lowering medications lysosomal acid lipase deficiency lysosomal storage disease
Online Access:	https://www.dovepress.com/lysosomal-acid-lipase-deficiency-therapeutic-options-peer-reviewed-article-DDDT

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