Gene therapy for Friedreich ataxia: Too much, too little, or just right?

Bibliographic Details
Main Author: R. Mark Payne
Format: Article
Language:English
Published: Elsevier 2022-06-01
Series:Molecular Therapy: Methods & Clinical Development
Online Access:http://www.sciencedirect.com/science/article/pii/S2329050122000249
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author R. Mark Payne
author_facet R. Mark Payne
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spelling doaj.art-2104f12b1d9b457ca6348d73b176f0972022-12-21T19:58:15ZengElsevierMolecular Therapy: Methods & Clinical Development2329-05012022-06-012512Gene therapy for Friedreich ataxia: Too much, too little, or just right?R. Mark Payne0Indiana University School of Medicine, Wells Center for Pediatric Research, 1044 West Walnut, R4302b, Indianapolis, IN 46202, USA; Corresponding author R. Mark Payne, MD, Indiana University School of Medicine, Wells Center for Pediatric Research, 1044 West Walnut, R4302b, Indianapolis, IN 46202, USA.http://www.sciencedirect.com/science/article/pii/S2329050122000249
spellingShingle R. Mark Payne
Gene therapy for Friedreich ataxia: Too much, too little, or just right?
Molecular Therapy: Methods & Clinical Development
title Gene therapy for Friedreich ataxia: Too much, too little, or just right?
title_full Gene therapy for Friedreich ataxia: Too much, too little, or just right?
title_fullStr Gene therapy for Friedreich ataxia: Too much, too little, or just right?
title_full_unstemmed Gene therapy for Friedreich ataxia: Too much, too little, or just right?
title_short Gene therapy for Friedreich ataxia: Too much, too little, or just right?
title_sort gene therapy for friedreich ataxia too much too little or just right
url http://www.sciencedirect.com/science/article/pii/S2329050122000249
work_keys_str_mv AT rmarkpayne genetherapyforfriedreichataxiatoomuchtoolittleorjustright