Emerging therapies for hemophilia: controversies and unanswered questions [version 1; referees: 4 approved]

Emerging therapies for hemophilia: controversies and unanswered questions [version 1; referees: 4 approved]

Several new therapies for hemophilia have emerged in recent years. These strategies range from extended half-life factor replacement products and non-factor options with improved pharmacokinetic profiles to gene therapy aiming for phenotypic cure. While these products have the potential to change he...

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Bibliographic Details
Main Authors:	Valder R. Arruda, Bhavya S. Doshi, Benjamin J. Samelson-Jones
Format:	Article
Language:	English
Published:	F1000 Research Ltd 2018-04-01
Series:	F1000Research
Online Access:	https://f1000research.com/articles/7-489/v1

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