A Rational Approach to Drug Repositioning in β-thalassemia: Induction of Fetal Hemoglobin by Established Drugs [version 3; peer review: 2 approved]
Drug repositioning and the relevance of orphan drug designation for β-thalassemia is reviewed. Drug repositioning and similar terms ('drug repurposing', 'drug reprofiling', 'drug redirecting', ‘drug rescue’, ‘drug re-tasking’ and/or 'drug rediscovery') have ga...
Main Authors: | Alessia Finotti, Ilaria Lampronti, Roberto Gambari, Cristina Zuccato, Marco Prosdocimi, Monica Borgatti, Lucia Carmela Cosenza |
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Format: | Article |
Language: | English |
Published: |
Wellcome
2022-08-01
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Series: | Wellcome Open Research |
Subjects: | |
Online Access: | https://wellcomeopenresearch.org/articles/7-150/v3 |
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