Therapeutic genome editing of an aberrant splice site in β-thalassemia by CRISPR/Cas9 with multiple sgRNAs

Bibliographic Details
Main Authors: Fei Yang, Shuqian Xu, Chao Huang, Zhiqiang Shao, Yuefen Hu, Yang Yang, Yongrong Lai, Qing Ke, Dan Liang, Yuxuan Wu
Format: Article
Language:English
Published: KeAi Communications Co., Ltd. 2024-01-01
Series:Genes and Diseases
Online Access:http://www.sciencedirect.com/science/article/pii/S2352304223000302