Prime Editing for Inherited Retinal Diseases
Inherited retinal diseases (IRDs) are chronic, hereditary disorders that lead to progressive degeneration of the retina. Disease etiology originates from a genetic mutation—inherited or de novo—with a majority of IRDs resulting from point mutations. Given the plethora of IRDs, to date, mutations tha...
Main Authors: | Bruna Lopes da Costa, Sarah R. Levi, Eric Eulau, Yi-Ting Tsai, Peter M. J. Quinn |
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Format: | Article |
Language: | English |
Published: |
Frontiers Media S.A.
2021-11-01
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Series: | Frontiers in Genome Editing |
Subjects: | |
Online Access: | https://www.frontiersin.org/articles/10.3389/fgeed.2021.775330/full |
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