Safety and efficacy of trofinetide in Rett syndrome: a systematic review and meta-analysis of randomized controlled trials

Safety and efficacy of trofinetide in Rett syndrome: a systematic review and meta-analysis of randomized controlled trials

Abstract Introduction Rett syndrome is a rare genetic neurodevelopmental disorder that predominantly impacts females. It presents with loss of acquired skills, impaired communication, and stereotypic hand movements. Given the limited treatment options for Rett syndrome, there is a dire need for effe...

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Bibliographic Details
Main Authors: Abdallah Abbas, Aya M Fayoud, Mostafa Hossam El Din Moawad, Abdullah Ashraf Hamad, Heba Hamouda, Eman A. Fouad
Format: Article
Language:English
Published: BMC 2024-03-01
Series:BMC Pediatrics
Subjects:
Daybue
Neurodevelopmental disorder
Rett syndrome
Trofinetide
Online Access:https://doi.org/10.1186/s12887-024-04526-3

Internet

https://doi.org/10.1186/s12887-024-04526-3

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