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O02: Baseline characteristics of a real-world population with alpha-mannosidosis: Insights from the SPARKLE Registry*

O02: Baseline characteristics of a real-world population with alpha-mannosidosis: Insights from the SPARKLE Registry*

Bibliographic Details
Main Authors: Nicole Muschol, Nathalie Guffon, Andrea Ballabeni, Line Borgwardt, Allan Lund, Mercedes Gil-Campos, Francesca Dona, Julia Hennermann
Format: Article
Language:English
Published: Elsevier 2023-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774423000031
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ISSN:2949-7744

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