Nanomedicine for Gene Delivery and Drug Repurposing in the Treatment of Muscular Dystrophies

Nanomedicine for Gene Delivery and Drug Repurposing in the Treatment of Muscular Dystrophies

Muscular Dystrophies (MDs) are a group of rare inherited genetic muscular pathologies encompassing a variety of clinical phenotypes, gene mutations and mechanisms of disease. MDs undergo progressive skeletal muscle degeneration causing severe health problems that lead to poor life quality, disabilit...

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Bibliographic Details
Main Authors: Ilaria Andreana, Mathieu Repellin, Flavia Carton, David Kryza, Stéphanie Briançon, Bénédicte Chazaud, Rémi Mounier, Silvia Arpicco, Manuela Malatesta, Barbara Stella, Giovanna Lollo
Format: Article
Language:English
Published: MDPI AG 2021-02-01
Series:Pharmaceutics
Subjects:
nanoparticles
Duchenne Muscular Dystrophy
myotonic dystrophy
antisense oligonucleotides
small molecules
CRISPR/Cas9
Online Access:https://www.mdpi.com/1999-4923/13/2/278

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