Gene therapy for selected neuromuscular and trinucleotide repeat disorders – An insight to subsume South Asia for multicenter clinical trials

Gene therapy for selected neuromuscular and trinucleotide repeat disorders – An insight to subsume South Asia for multicenter clinical trials

Background: In this article, the authors discuss how they utilized the genetic mutation data in Sri Lankan Duchenne muscular dystrophy (DMD), Spinal muscular atrophy (SMA), Spinocerebellar ataxia (SCA) and Huntington’s disease (HD) patients and compare the available literature from South Asian count...

Πλήρης περιγραφή

Λεπτομέρειες βιβλιογραφικής εγγραφής
Κύριοι συγγραφείς: Nalaka Wijekoon, Lakmal Gonawala, Pyara Ratnayake, Darshana Sirisena, Harsha Gunasekara, Athula Dissanayake, Sunethra Senanayake, Ajantha Keshavaraj, Yetrib Hathout, Harry W.M. Steinbusch, Chandra Mohan, Ashwin Dalal, Eric Hoffman, K.Ranil D de Silva
Μορφή: Άρθρο
Γλώσσα:English
Έκδοση: Elsevier 2023-06-01
Σειρά:IBRO Neuroscience Reports
Θέματα:
Indian Sub-continent
Developing Countries
Neurogenetic Disorders
Bio Bank
Duchenne Muscular Dystrophy
Spinal Muscular Atrophy
Διαθέσιμο Online:http://www.sciencedirect.com/science/article/pii/S266724212300009X

Διαδίκτυο

http://www.sciencedirect.com/science/article/pii/S266724212300009X

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