Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C

Bibliographic Details
Main Author: Raimondo De Cristofaro
Format: Article
Language:English
Published: Elsevier 2023-09-01
Series:Molecular Therapy: Nucleic Acids
Online Access:http://www.sciencedirect.com/science/article/pii/S2162253123002159