Gene therapy in hereditary retinal dystrophy

Gene therapy in hereditary retinal dystrophy

Hereditary retinal dystrophies (HRDs), such as retinitis pigmentosa, Leber's congenital amaurosis (LCA), Usher syndrome, and retinoschisis, are a group of genetic retinal disorders exhibiting both genetic and phenotypic heterogeneity. Symptoms include progressive retinal degeneration and constr...

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Bibliographic Details
Main Authors:	Jia-Ying Chien, Shun-Ping Huang
Format:	Article
Language:	English
Published:	Wolters Kluwer Medknow Publications 2022-01-01
Series:	Tzu-Chi Medical Journal
Subjects:	antisense oligonucleotides clustered regularly interspaced short palindromic repeat/cas system gene therapy optogenetics retinal dystrophy
Online Access:	http://www.tcmjmed.com/article.asp?issn=1016-3190;year=2022;volume=34;issue=4;spage=367;epage=372;aulast=Chien

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