P016: Results of an open-label, single-center, clinical study evaluating the safety and tolerability of pentosan polysulfate sodium in mucopolysaccharidosis I subjects
Main Authors: | Curtis Gravance, Drago Bratkovic, David Ketteridge, Michael Imperiale, Ravi Krishnan, Divya Navuru |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2023-01-01
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Series: | Genetics in Medicine Open |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2949774423000262 |
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