P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS
| Main Authors: | , , , , , , , , |
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| Format: | Article |
| Language: | English |
| Published: |
Wiley
2022-01-01
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| Series: | HemaSphere |
| Online Access: | http://journals.lww.com/10.1097/01.HS9.0000821508.47147.52 |
| _version_ | 1797283163844640768 |
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| author | M Badat P Hua S Mettananda C Fisher N Roy S Rice A Roy D Higgs J Davies |
| author_facet | M Badat P Hua S Mettananda C Fisher N Roy S Rice A Roy D Higgs J Davies |
| author_sort | M Badat |
| collection | DOAJ |
| first_indexed | 2024-03-07T17:27:07Z |
| format | Article |
| id | doaj.art-5dc91feaa86f47c386ac96f4be191392 |
| institution | Directory Open Access Journal |
| issn | 2572-9241 |
| language | English |
| last_indexed | 2024-03-07T17:27:07Z |
| publishDate | 2022-01-01 |
| publisher | Wiley |
| record_format | Article |
| series | HemaSphere |
| spelling | doaj.art-5dc91feaa86f47c386ac96f4be1913922024-03-02T18:51:39ZengWileyHemaSphere2572-92412022-01-016192010.1097/01.HS9.0000821508.47147.52202201001-00036P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLSM Badat0P Hua1S Mettananda2C Fisher3N Roy4S Rice5A Roy6D Higgs7J Davies81 Barts Health NHS Trust, London, UNITED KINGDOM2 Weatherall Institute of Molecular Medicine, Oxford, UNITED KINGDOM3 University of Kelaniya, Ragama, SRI LANKA2 Weatherall Institute of Molecular Medicine, Oxford, UNITED KINGDOM4 Dept Haematology, Oxford University Hospitals NHS Trust, Oxford, UNITED KINGDOM2 Weatherall Institute of Molecular Medicine, Oxford, UNITED KINGDOM2 Weatherall Institute of Molecular Medicine, Oxford, UNITED KINGDOM2 Weatherall Institute of Molecular Medicine, Oxford, UNITED KINGDOM2 Weatherall Institute of Molecular Medicine, Oxford, UNITED KINGDOMhttp://journals.lww.com/10.1097/01.HS9.0000821508.47147.52 |
| spellingShingle | M Badat P Hua S Mettananda C Fisher N Roy S Rice A Roy D Higgs J Davies P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS HemaSphere |
| title | P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS |
| title_full | P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS |
| title_fullStr | P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS |
| title_full_unstemmed | P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS |
| title_short | P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS |
| title_sort | p104 base editing repairs the hbe mutation restoring the production of normal globin chains in severe hbe β thalassemia patient hematopoietic stem and erythroid cells |
| url | http://journals.lww.com/10.1097/01.HS9.0000821508.47147.52 |
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