Ocular Gene Therapy with Adeno-associated Virus Vectors: Current Outlook for Patients and Researchers
In this “Perspective”, we discuss ocular gene therapy – the patient's perspective, the various strategies of gene replacement and gene editing, the place of adeno-associated virus vectors, routes of delivery to the eye and the remaining question - “why does immunity continue to limit efficacy?”...
Main Authors: | Geoffrey A. Casey, Kimberly M. Papp, Ian M. MacDonald |
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Format: | Article |
Language: | English |
Published: |
Knowledge E
2020-08-01
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Series: | Journal of Ophthalmic & Vision Research |
Online Access: | https://doi.org/10.18502/jovr.v15i3.7457 |
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