P232: Translational advancements in Cockayne syndrome: Preparing for an AAV-mediated hERCC8 gene therapy trial

P232: Translational advancements in Cockayne syndrome: Preparing for an AAV-mediated hERCC8 gene therapy trial

Bibliographic Details
Main Authors:	Robert Thompson, Florian Eichler
Format:	Article
Language:	English
Published:	Elsevier 2024-01-01
Series:	Genetics in Medicine Open
Online Access:	http://www.sciencedirect.com/science/article/pii/S2949774424002747

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